LUXTURNA® (voretigene neparvovec-rzyl) - Inherited Retinal …
LUXTURNA (voretigene neparvovec-rzyl) is a prescription gene therapy product used for the treatment of patients with inherited retinal disease due to mutations in both copies of the …
What is LUXTURNA? - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA is the first prescription gene therapy product to help improve functional vision in patients with an inherited retinal disease (IRD) due to a mutation in their RPE65 gene. It is a …
How does LUXTURNA work? - LUXTURNA® (voretigene …
One approach to gene therapy is delivering a new or functional gene into a cell, which is how LUXTURNA works. Working to restore the visual cycle The visual cycle is a process that …
Take your first step - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA (voretigene neparvovec-rzyl) is a prescription gene therapy product used for the treatment of patients with inherited retinal disease due to mutations in both copies of the …
Patient resources - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA is a one-time gene therapy for patients 12 months of age and older. LUXTURNA is not recommended for patients younger than 12 months of age because the retina is still …
Find a specialist - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA (voretigene neparvovec-rzyl) is a prescription gene therapy product used for the treatment of patients with inherited retinal disease due to mutations in both copies of the …
LUXTURNA (voretigene neparvovec-rzyl) is an adeno-associated virus vector-based gene therapy indicated for the treatment of patients with confirmed biallelic RPE65 mutation …
Site Map - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA (voretigene neparvovec-rzyl) is a prescription gene therapy product used for the treatment of patients with inherited retinal disease due to mutations in both copies of the …
Patient stories - LUXTURNA® (voretigene neparvovec-rzyl)
Dealing with an inherited retinal disease (IRD) can be difficult and navigating treatment options can be complicated. Check out the stories below to see how Spark ® Therapeutics was able …
Stay up to date - LUXTURNA® (voretigene neparvovec-rzyl)
LUXTURNA (voretigene neparvovec-rzyl) is a prescription gene therapy product used for the treatment of patients with inherited retinal disease due to mutations in both copies of the …